Pages that link to "Q36897347"
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The following pages link to Effective rescue of dystrophin improves cardiac function in dystrophin-deficient mice by a modified morpholino oligomer (Q36897347):
Displaying 50 items.
- Peptides for nucleic acid delivery (Q26746968) (← links)
- A chemical view of oligonucleotides for exon skipping and related drug applications (Q26863684) (← links)
- Proteomic profiling of the dystrophin-deficient mdx phenocopy of dystrophinopathy-associated cardiomyopathy (Q27006945) (← links)
- Antisense oligonucleotides: treating neurodegeneration at the level of RNA (Q27007056) (← links)
- Splicing therapy for neuromuscular disease (Q27009581) (← links)
- Current understanding of molecular pathology and treatment of cardiomyopathy in duchenne muscular dystrophy (Q28082625) (← links)
- Animal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapy (Q28084979) (← links)
- Targeted skipping of human dystrophin exons in transgenic mouse model systemically for antisense drug development (Q28478166) (← links)
- Silencing disease genes in the laboratory and the clinic (Q29039090) (← links)
- Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping (Q30493685) (← links)
- Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping (Q30514014) (← links)
- Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice (Q30626615) (← links)
- Guanine analogues enhance antisense oligonucleotide-induced exon skipping in dystrophin gene in vitro and in vivo (Q33525253) (← links)
- Long-term improvement in mdx cardiomyopathy after therapy with peptide-conjugated morpholino oligomers (Q33573648) (← links)
- Effects of systemic multiexon skipping with peptide-conjugated morpholinos in the heart of a dog model of Duchenne muscular dystrophy (Q33863805) (← links)
- Context Dependent Effects of Chimeric Peptide Morpholino Conjugates Contribute to Dystrophin Exon-skipping Efficiency (Q33637391) (← links)
- Evaluation of Tris[2-(acryloyloxy)ethyl]isocyanurate cross-linked polyethylenimine as antisense morpholino oligomer delivery vehicle in cell culture and dystrophic mdx mice (Q33637696) (← links)
- Long-term treatment with naproxcinod significantly improves skeletal and cardiac disease phenotype in the mdx mouse model of dystrophy (Q33649312) (← links)
- Octa-guanidine morpholino restores dystrophin expression in cardiac and skeletal muscles and ameliorates pathology in dystrophic mdx mice (Q33713525) (← links)
- Chronic administration of membrane sealant prevents severe cardiac injury and ventricular dilatation in dystrophic dogs (Q33755416) (← links)
- Emerging genetic therapies to treat Duchenne muscular dystrophy (Q33796975) (← links)
- Gene and cell-mediated therapies for muscular dystrophy. (Q33831193) (← links)
- A steric blocker of translation elongation inhibits IGF‐1R expression and cell transformation (Q33845618) (← links)
- Proteomic Profiling of the Dystrophin-Deficient MDX Heart Reveals Drastically Altered Levels of Key Metabolic and Contractile Proteins. (Q33871052) (← links)
- Gene knockdowns in adult animals: PPMOs and vivo-morpholinos (Q34016744) (← links)
- Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model (Q34117470) (← links)
- In vivo MRI characterization of progressive cardiac dysfunction in the mdx mouse model of muscular dystrophy. (Q34123466) (← links)
- Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice (Q34204198) (← links)
- RNA therapeutics: beyond RNA interference and antisense oligonucleotides (Q34248493) (← links)
- Sildenafil reverses cardiac dysfunction in the mdx mouse model of Duchenne muscular dystrophy. (Q34279254) (← links)
- Local in vivo GSK3β knockdown promotes pancreatic β cell and acinar cell regeneration in 90% pancreatectomized rat (Q34290057) (← links)
- Anti-tumor activity of splice-switching oligonucleotides (Q34401490) (← links)
- The status of exon skipping as a therapeutic approach to duchenne muscular dystrophy (Q34473336) (← links)
- Chronic systemic therapy with low-dose morpholino oligomers ameliorates the pathology and normalizes locomotor behavior in mdx mice (Q34556906) (← links)
- Antisense therapy in neurology (Q34608717) (← links)
- One-year treatment of morpholino antisense oligomer improves skeletal and cardiac muscle functions in dystrophic mdx mice (Q34621772) (← links)
- Inhibition of nonsense-mediated mRNA decay by antisense morpholino oligonucleotides restores functional expression of hERG nonsense and frameshift mutations in long-QT syndrome (Q34626870) (← links)
- Progress in muscular dystrophy research with special emphasis on gene therapy (Q34734708) (← links)
- Therapeutic approaches to muscular dystrophy. (Q34982869) (← links)
- Current status of pharmaceutical and genetic therapeutic approaches to treat DMD. (Q34994545) (← links)
- Duchenne muscular dystrophy gene therapy: Lost in translation? (Q35052506) (← links)
- Restoring dystrophin expression in duchenne muscular dystrophy muscle progress in exon skipping and stop codon read through (Q35072755) (← links)
- Pip5 transduction peptides direct high efficiency oligonucleotide-mediated dystrophin exon skipping in heart and phenotypic correction in mdx mice. (Q35084227) (← links)
- Targeted excision of VCP R155H mutation by Cre-LoxP technology as a promising therapeutic strategy for valosin-containing protein disease (Q35110776) (← links)
- Arginine-rich cell-penetrating peptide dramatically enhances AMO-mediated ATM aberrant splicing correction and enables delivery to brain and cerebellum. (Q35119681) (← links)
- SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice (Q35183186) (← links)
- Parallel synthesis of cell-penetrating peptide conjugates of PMO toward exon skipping enhancement in Duchenne muscular dystrophy. (Q35439476) (← links)
- The evolution of heart gene delivery vectors (Q35799722) (← links)
- The use of urinary and kidney SILAM proteomics to monitor kidney response to high dose morpholino oligonucleotides in the mdx mouse (Q35881677) (← links)
- Cationic polyelectrolyte-mediated delivery of antisense morpholino oligonucleotides for exon-skipping in vitro and in mdx mice. (Q36036988) (← links)