Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX. (Q45886876)

17 December 2017

title

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX. (English)

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17 December 2017

main subject

hemophilia

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coagulation factor IX

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4

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author name string

Bigger BW

1

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Siapati EK

2

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Mistry A

3

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Nivsarkar MS

5

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Jacobs L

6

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Perrett R

7

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Holder MV

8

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Ridler C

9

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Kemball-Cook G

10

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Ali RR

11

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Forbes SJ

12

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Coutelle C

13

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Wright N

14

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Alison M

15

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Thrasher AJ

16

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Bonnet D

17

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Themis M

18

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publication date

1 January 2006

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17 December 2017

published in

Gene Therapy

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17 December 2017

volume

13

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17 December 2017

issue

2

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17 December 2017

page(s)

117-126

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17 December 2017

Haemophilia B mutations in Sweden: a population-based study of mutational heterogeneity

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Retroviral Transfer of Donor MHC Class I or MHC Class II Genes into Recipient Bone Marrow Cells Can Induce Operational Tolerance to AlloantigensIn Vivo

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Engraftment of retroviral EGFP-transduced bone marrow in mice prevents rejection of EGFP-transgenic skin grafts

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Myeloablation is not required to select and maintain expression of the drug-resistance gene, mutant MGMT, in primary and secondary recipients

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Induction of stable long-term mixed hematopoietic chimerism following nonmyeloablative conditioning with T cell-depleting antibodies, cyclophosphamide, and thymic irradiation leads to donor-specific in vitro and in vivo tolerance

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inferred from DOI database lookup

7 January 2021

based on heuristic

Engraftment assessment in human and mouse liver tissue after sex-mismatched liver cell transplantation by real-time quantitative PCR for Y chromosome sequences

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302638

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/SJ.GT.3302638

1 reference

17 December 2017

Dimensions Publication ID

1014126699

0 references

1 reference

17 December 2017