A prospective one-year natural history study of mucopolysaccharidosis types IIIA and IIIB: Implications for clinical trial design. (Q45857959)

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22 March 2020

title

A prospective one-year natural history study of mucopolysaccharidosis types IIIA and IIIB: Implications for clinical trial design (English)

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14

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Linda Lowes

11

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22 March 2020

author name string

K V Truxal

1

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22 March 2020

H Fu

2

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D M McCarty

3

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K A McNally

4

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K L Kunkler

5

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N A Zumberge

6

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L Martin

7

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S C Aylward

8

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L N Alfano

9

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K M Berry

10

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M Corridore

12

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C McKee

13

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K M Flanigan

15

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publication date

18 August 2016

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Molecular Genetics and Metabolism

22 March 2020

published in

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volume

119

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issue

3

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22 March 2020

page(s)

239-248

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Prevalence rates of mucopolysaccharidoses in Poland

22 March 2020

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Mucopolysaccharidosis Type III (Sanfilippo Syndrome): Emerging Treatment Strategies

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7 January 2021

Identifiers

DOI

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release_ilsotwytlbe2xgjlqhxr76w5uu

22 March 2020

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mapped directly with Wikidata item

24 November 2022

based on heuristic

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