Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients. (Q40218144)

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20 December 2019

title

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients (English)

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20 December 2019

2

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20 December 2019

Alessandro Aiuti

8

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20 December 2019

Maria Grazia Roncarolo

11

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20 December 2019

author name string

S Charrier

1

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20 December 2019

S Scaramuzza

3

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20 December 2019

L Jeanson-Leh

4

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20 December 2019

M P Blundell

5

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20 December 2019

O Danos

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20 December 2019

F Cattaneo

7

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20 December 2019

R Eckenberg

9

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20 December 2019

A J Thrasher

10

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20 December 2019

A Galy

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20 December 2019

publication date

19 October 2006

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20 December 2019

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20 December 2019

volume

14

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20 December 2019

issue

5

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20 December 2019

page(s)

415-428

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The Wiskott-Aldrich syndrome protein: forging the link between actin and cell activation

20 December 2019

cites work

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Mechanisms of WASp-mediated hematologic and immunologic disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Mechanism of recruitment of WASP to the immunological synapse and of its activation following TCR ligation

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Wiskott-Aldrich syndrome protein regulates lipid raft dynamics during immunological synapse formation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Retrovirus-mediated WASP gene transfer corrects defective actin polymerization in B cell lines from Wiskott-Aldrich syndrome patients carrying 'null' mutations.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Retrovirus-mediated WASP gene transfer corrects Wiskott-Aldrich syndrome T-cell dysfunction

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Gene therapy for Wiskott-Aldrich syndrome: rescue of T-cell signaling and amelioration of colitis upon transplantation of retrovirally transduced hematopoietic stem cells in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Functional correction of T cells derived from patients with the Wiskott–Aldrich syndrome (WAS) by transduction with an oncoretroviral vector encoding the WAS protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Lentiviral vector-mediated gene transfer in T cells from Wiskott-Aldrich syndrome patients leads to functional correction.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Lentiviral vectors transcriptionally targeted to hematopoietic cells by WASP gene proximal promoter sequences.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

High-level transduction and gene expression in hematopoietic repopulating cells using a human immunodeficiency [correction of imunodeficiency] virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

A partial down-regulation of WASP is sufficient to inhibit podosome formation in dendritic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

WASp in immune-system organization and function

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Wiskott-Aldrich syndrome protein and the cytoskeletal dynamics of dendritic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Macrophages of patients with X-linked thrombocytopenia display an attenuated Wiskott-Aldrich syndrome phenotype

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Activation of monocytes via the CD14 receptor leads to the enhanced lentiviral transduction of immature dendritic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

The identification and characterization of two promoters and the complete genomic sequence for the Wiskott-Aldrich syndrome gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

JASPAR: an open-access database for eukaryotic transcription factor binding profiles

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

TFBS: Computational framework for transcription factor binding site analysis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Defects in T-cell-mediated immunity to influenza virus in murine Wiskott-Aldrich syndrome are corrected by oncoretroviral vector-mediated gene transfer into repopulating hematopoietic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G0/G1 human hematopoietic stem cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Efficiency of transduction of highly purified murine hematopoietic stem cells by lentiviral and oncoretroviral vectors under conditions of minimal in vitro manipulation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Promoter trapping reveals significant differences in integration site selection between MLV and HIV vectors in primary hematopoietic cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

One step screening of retroviral producer clones by real time quantitative PCR.

21 January 2018

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https://api.crossref.org/works/10.1038/SJ.GT.3302863

The Wiskott-Aldrich syndrome

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

7 January 2021

Restoration of podosomes and chemotaxis in Wiskott-Aldrich syndrome macrophages following induced expression of WASp

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

7 January 2021

WASp deficiency in mice results in failure to form osteoclast sealing zones and defects in bone resorption

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

7 January 2021

A third-generation lentivirus vector with a conditional packaging system

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302863

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302863

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17051251 AND SRC:MED&resulttype=core&format=json

Dimensions Publication ID

20 December 2019

1031820665

0 references

1 reference