Characterization of pre- and post-treatment pathology after enzyme replacement therapy for Pompe disease (Q39773493)
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English | Characterization of pre- and post-treatment pathology after enzyme replacement therapy for Pompe disease |
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Characterization of pre- and post-treatment pathology after enzyme replacement therapy for Pompe disease (English)
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Beth L Thurberg
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Colleen Lynch Maloney
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Charles Vaccaro
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Kendra Afonso
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Anne Chun-Hui Tsai
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Edward Bossen
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Priya S Kishnani
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Michael O'Callaghan
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30 October 2006
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86
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12
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1208-1220
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