Neural Stem Cell Transplantation as a Therapeutic Approach for Treating Lysosomal Storage Diseases (Q37929618)

25 August 2017

1 reference

title

Neural stem cell transplantation as a therapeutic approach for treating lysosomal storage diseases (English)

1 reference

25 August 2017

Neural Stem Cell Transplantation as a Therapeutic Approach for Treating Lysosomal Storage Diseases (English)

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

12 December 2024

1 reference

stem cell transplantation

1 reference

Lamya S. Shihabuddin

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

12 December 2024

Seng H. Cheng

series ordinal

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

12 December 2024

language of work or name

English

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National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=21904790

12 December 2024

publication date

1 October 2011

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25 August 2017

October 2011

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National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=21904790

full work available at URL

12 December 2024

https://link.springer.com/content/pdf/10.1007/s13311-011-0067-8.pdf

Portable Document Format

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

https://europepmc.org/articles/PMC3250293

12 December 2024

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

https://europepmc.org/articles/PMC3250293?pdf=render

12 December 2024

Portable Document Format

content deliverer

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

https://doi.org/10.1007/s13311-011-0067-8

12 December 2024

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21904790

http://link.springer.com/content/pdf/10.1007/s13311-011-0067-8.pdf

12 December 2024

Portable Document Format

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

http://link.springer.com/article/10.1007/s13311-011-0067-8/fulltext.html

12 December 2024

HyperText Markup Language

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

https://api.elsevier.com/content/article/PII:S1878747923017907?httpAccept=text/xml

12 December 2024

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

https://api.elsevier.com/content/article/PII:S1878747923017907?httpAccept=text/plain

12 December 2024

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

http://link.springer.com/content/pdf/10.1007/s13311-011-0067-8

12 December 2024

1 reference

https://api.crossref.org/works/10.1007/S13311-011-0067-8

12 December 2024

1 reference

25 August 2017

8

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25 August 2017

4

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25 August 2017

659-667

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Direct reprogramming of mouse fibroblasts to neural progenitors

25 August 2017

1 reference

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Neural stem cell transplantation benefits a monogenic neurometabolic disorder during the symptomatic phase of disease

6 September 2017

1 reference

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6 September 2017

1 reference

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Treating lysosomal storage disorders: current practice and future prospects

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Stem cell therapies for the lysosomal storage diseases - the quintessential neurodegenerative diseases

6 September 2017

1 reference

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Treatment of late infantile neuronal ceroid lipofuscinosis by CNS administration of a serotype 2 adeno-associated virus expressing CLN2 cDNA.

6 September 2017

1 reference

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Central nervous system therapy for lysosomal storage disorders

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

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6 September 2017

1 reference

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6 September 2017

1 reference

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6 September 2017

1 reference

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Stem cells in the umbilical cord

6 September 2017

1 reference

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Neuronal ceroid lipofuscinoses therapeutic strategies: past, present and future

6 September 2017

1 reference

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Cell replacement therapy in neurological disease

6 September 2017

1 reference

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6 September 2017

1 reference

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6 September 2017

1 reference

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6 September 2017

1 reference

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Niche-independent symmetrical self-renewal of a mammalian tissue stem cell

6 September 2017

1 reference

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A new human somatic stem cell from placental cord blood with intrinsic pluripotent differentiation potential

6 September 2017

1 reference

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Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells

6 September 2017

1 reference

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Isolation and characterization of neural progenitor cells from post-mortem human cortex

6 September 2017

1 reference

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Neuroectodermal differentiation from mouse multipotent adult progenitor cells

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Enzyme replacement and enhancement therapies: lessons from lysosomal disorders

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Repairing the damaged spinal cord: a summary of our early success with embryonic stem cell transplantation and remyelination

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Human neural stem and progenitor cells: in vitro and in vivo properties, and potential for gene therapy and cell replacement in the CNS.

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Intracerebral transplantation of mesenchymal stem cells into acid sphingomyelinase-deficient mice delays the onset of neurological abnormalities and extends their life span.

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

The development of neural stem cells

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Direct isolation of human central nervous system stem cells

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Sphingomyelin-cholesterol interactions in biological and model membranes

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Mammalian neural stem cells

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Establishment and properties of neural stem cell clones: plasticity in vitro and in vivo

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Human neural stem cells: isolation, expansion and transplantation

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Prevalence of lysosomal storage disorders

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Embryonic stem cell lines derived from human blastocysts

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

In vitro -generated neural precursors participate in mammalian brain development

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Survival and differentiation of adult neuronal progenitor cells transplanted to the adult brain.

6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

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6 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

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6 September 2017

1 reference

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6 September 2017

1 reference

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Transdetermination: a new trend in cellular reprogramming

6 September 2017

1 reference

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Clonal amniotic fluid-derived stem cells express characteristics of both mesenchymal and neural stem cells

6 September 2017

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Human embryonic stem cells differentiate into oligodendrocytes in high purity and myelinate after spinal cord transplantation

14 September 2017

1 reference

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14 September 2017

1 reference

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28 September 2017

1 reference

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1 reference

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28 September 2017

1 reference

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28 September 2017

1 reference

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28 September 2017

1 reference

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Neural progenitor cell engraftment corrects lysosomal storage throughout the MPS VII mouse brain

28 September 2017

1 reference

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28 September 2017

1 reference

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Multipotent CNS stem cells are present in the adult mammalian spinal cord and ventricular neuroaxis.

23 June 2018

1 reference

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Quantitative correlation between the residual activity of beta-hexosaminidase A and arylsulfatase A and the severity of the resulting lysosomal storage disease

23 June 2018

1 reference

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23 June 2018

1 reference

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1 September 2018

1 reference

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1 September 2018

1 reference

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1 September 2018

1 reference

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1 September 2018

1 reference

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Intracerebral transplantation of adult mouse neural progenitor cells into the Niemann-Pick-A mouse leads to a marked decrease in lysosomal storage pathology.

1 September 2018

1 reference

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1 September 2018

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1 September 2018

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1 September 2018

1 reference

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1 September 2018

1 reference

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Long-term expression of beta-glucuronidase by genetically modified human neural progenitor cells grafted into the mouse central nervous system.

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Acid sphingomyelinase-deficient macrophages have defective cholesterol trafficking and efflux

1 September 2018

1 reference

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Patterned cerebellar Purkinje cell death in a transgenic mouse model of Niemann Pick type A/B disease

1 September 2018

1 reference

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1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Engraftable human neural stem cells respond to developmental cues, replace neurons, and express foreign genes.

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3250293

Multipotential stem cells from the adult mouse brain proliferate and self-renew in response to basic fibroblast growth factor.

1 September 2018

1 reference

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12 December 2020

Human neural precursor cells express low levels of telomerase in vitro and show diminishing cell proliferation with extensive axonal outgrowth following transplantation

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Sanfilippo disease type B: enzyme replacement and metabolic correction in cultured fibroblasts

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Lysenin, a Novel Sphingomyelin-specific Binding Protein

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Neural stem cells and their use as therapeutic tool in neurological disorders

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Cell biology. Ready or not? Human ES cells head toward the clinic

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12 December 2020

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12 December 2020

Identifiers

1 reference

25 August 2017

1 reference

25 August 2017

1 reference