CPP-Directed Oligonucleotide Exon Skipping in Animal Models of Duchenne Muscular Dystrophy (Q37807346)

23 August 2017

title

CPP-directed oligonucleotide exon skipping in animal models of Duchenne muscular dystrophy (English)

1 reference

23 August 2017

CPP-Directed Oligonucleotide Exon Skipping in Animal Models of Duchenne Muscular Dystrophy (English)

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

21 August 2024

4

Matthew Wood

1 reference

23 August 2017

HaiFang Yin

1

1 reference

23 August 2017

Hong Moulton

2

1 reference

23 August 2017

Corinne Betts

3

1 reference

23 August 2017

Matthew Wood

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC:MED AND EXT_ID:21053140

21 August 2024

language of work or name

English

0 references

publication date

1 January 2011

1 reference

full work available at URL

23 August 2017

number of pages

18

1 reference

based on heuristic

inferred from page(s)

https://link.springer.com/content/pdf/10.1007/978-1-60761-919-2_23

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Methods in Molecular Biology

21 August 2024

published in

1 reference

23 August 2017

volume

683

1 reference

23 August 2017

page(s)

321-338

1 reference

Molecular mechanisms of muscular dystrophies: old and new players

23 August 2017

cites work

1

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Dystrophin and mutations: one gene, several proteins, multiple phenotypes

21 August 2024

2

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Advances in Duchenne muscular dystrophy gene therapy

21 August 2024

3

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients.

21 August 2024

4

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

21 August 2024

5

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Sustained dystrophin expression induced by peptide-conjugated morpholino oligomers in the muscles of mdx mice.

21 August 2024

6

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

21 August 2024

7

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

21 August 2024

8

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

21 August 2024

9

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Effective rescue of dystrophin improves cardiac function in dystrophin-deficient mice by a modified morpholino oligomer

21 August 2024

10

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Effective exon skipping and restoration of dystrophin expression by peptide nucleic acid antisense oligonucleotides in mdx mice

21 August 2024

11

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function.

21 August 2024

12

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle

21 August 2024

13

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

21 August 2024

14

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Local dystrophin restoration with antisense oligonucleotide PRO051

21 August 2024

15

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations

21 August 2024

16

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Peptide-based delivery of nucleic acids: design, mechanism of uptake and applications to splice-correcting oligonucleotides

21 August 2024

17

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Octa-guanidine morpholino restores dystrophin expression in cardiac and skeletal muscles and ameliorates pathology in dystrophic mdx mice

21 August 2024

18

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Efficacy of systemic morpholino exon-skipping in Duchenne dystrophy dogs

21 August 2024

19

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

Improved cell-penetrating peptide-PNA conjugates for splicing redirection in HeLa cells and exon skipping in mdx mouse muscle.

21 August 2024

20

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

PNA-peptide conjugates as intracellular gene control agents

21 August 2024

21

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice.

21 August 2024

22

1 reference

https://api.crossref.org/works/10.1007/978-1-60761-919-2_23

21 August 2024

Identifiers

1 reference

23 August 2017

1 reference