Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice. (Q36545533)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18414684 AND SRC:MED&resulttype=core&format=json

5 January 2020

title

Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice (English)

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4

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Luisa Cutillo

11

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Alberto Auricchio

15

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1

Mariacarmela Allocca

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author name string

Monica Doria

2

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Marco Petrillo

3

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Maria Garcia-Hoyos

5

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Daniel Gibbs

6

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So Ra Kim

7

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Albert Maguire

8

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Tonia S Rex

9

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Umberto Di Vicino

10

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Janet R Sparrow

12

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David S Williams

13

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Jean Bennett

14

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language of work or name

English

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publication date

1 May 2008

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Journal of Clinical Investigation

5 January 2020

published in

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volume

118

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issue

5

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5 January 2020

page(s)

1955-1964

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Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors

5 January 2020

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30 September 2017

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30 September 2017

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30 September 2017

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Delayed dark-adaptation and lipofuscin accumulation in abcr /- mice: implications for involvement of ABCR in age-related macular degeneration

30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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30 September 2017

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28 June 2018

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Quantitative analysis of the packaging capacity of recombinant adeno-associated virus

28 June 2018

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Commentary: an aye for eye gene therapy

28 June 2018

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Specific and efficient transduction of Cochlear inner hair cells with recombinant adeno-associated virus type 3 vector

21 September 2018

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N-retinylidene-phosphatidylethanolamine is the preferred retinoid substrate for the photoreceptor-specific ABC transporter ABCA4 (ABCR).

21 September 2018

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Absolute configurational determination of an all-trans-retinal dimer isolated from photoreceptor outer segments

21 September 2018

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Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy.

21 September 2018

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Pharmacological regulation of protein expression from adeno-associated viral vectors in the eye.

21 September 2018

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Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model

21 September 2018

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21 September 2018

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Biochemical defects in ABCR protein variants associated with human retinopathies

21 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/18414684

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1172/JCI34316

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18414684 AND SRC:MED&resulttype=core&format=json

5 January 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:18414684 AND SRC:MED&resulttype=core&format=json

5 January 2020

PubMed publication ID

18414684

1 reference