Persistent expression of factor VIII in vivo following nonprimate lentiviral gene transfer (Q35848097)

10 August 2017

Persistent expression of factor VIII in vivo following nonprimate lentiviral gene transfer (English)

1 reference

10 August 2017

Paul B McCray

7

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author name string

Yubin Kang

1

1 reference

10 August 2017

Litao Xie

2

1 reference

10 August 2017

Diane Thi Tran

3

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10 August 2017

Colleen S Stein

4

1 reference

10 August 2017

Melissa Hickey

5

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10 August 2017

Beverly L Davidson

6

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10 August 2017

language of work or name

English

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publication date

10 May 2005

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10 August 2017

7

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inferred from page(s)

published in

Blood

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10 August 2017

106

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10 August 2017

5

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10 August 2017

1552-1558

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Towards the goal of prophylaxis: experience and treatment strategies from Sweden, France and Hungary

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1 reference

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Lentiviral vectors pseudotyped with baculovirus gp64 efficiently transduce mouse cells in vivo and show tropism restriction against hematopoietic cell types in vitro

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1 reference

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Bioengineering of coagulation factor VIII for improved secretion

11 July 2018

1 reference

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In vitro and in vivo gene delivery by recombinant baculoviruses.

11 July 2018

1 reference

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Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion

11 July 2018

1 reference

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Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

11 July 2018

1 reference

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Lentivirus vectors pseudotyped with filoviral envelope glycoproteins transduce airway epithelia from the apical surface independently of folate receptor alpha

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1 reference

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Large-scale production of pseudotyped lentiviral vectors using baculovirus GP64.

11 July 2018

1 reference

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In vivo gene transfer using a nonprimate lentiviral vector pseudotyped with Ross River Virus glycoproteins

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1 reference

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Transfer, incorporation, and substitution of envelope fusion proteins among members of the Baculoviridae, Orthomyxoviridae, and Metaviridae (insect retrovirus) families

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Systematic determination of the packaging limit of lentiviral vectors

11 July 2018

1 reference

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Generation and characterization of E1/E2a/E3/E4-deficient adenoviral vectors encoding human factor VIII.

11 July 2018

1 reference

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VSV-G pseudotyped lentiviral vector particles produced in human cells are inactivated by human serum

11 July 2018

1 reference

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Correlation between factor VIII genotype and inhibitor development in hemophilia A.

11 July 2018

1 reference

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Somatic integration and long-term transgene expression in normal and haemophilic mice using a DNA transposon system

11 July 2018

1 reference

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Sustained expression of human factor VIII in mice using a parvovirus-based vector.

11 July 2018

1 reference

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Animal testing of retroviral-mediated gene therapy for factor VIII deficiency

11 July 2018

1 reference

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Feline immunodeficiency virus vectors persistently transduce nondividing airway epithelia and correct the cystic fibrosis defect

11 July 2018

1 reference

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Short-term correction of factor VIII deficiency in a murine model of hemophilia A after delivery of adenovirus murine factor VIII in utero

11 July 2018

1 reference

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Advances toward gene therapy for hemophilia at the millennium

11 July 2018

1 reference

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Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

11 July 2018

1 reference

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Host cell receptor binding by baculovirus GP64 and kinetics of virion entry

11 July 2018

1 reference

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Minimum requirements for efficient transduction of dividing and nondividing cells by feline immunodeficiency virus vectors

11 July 2018

1 reference

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Baculovirus-mediated gene transfer into mammalian cells

11 July 2018

1 reference

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In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

11 July 2018

1 reference

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Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells

11 July 2018

1 reference

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Heterogeneity of the immune response to adenovirus-mediated factor VIII gene therapy in different inbred hemophilic mouse strains

11 July 2018

1 reference

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Thirty years of hemophilia treatment in the Netherlands, 1972-2001.

24 September 2018

1 reference

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Induction of antigen-specific CD4 T-cell anergy and deletion by in vivo viral gene transfer

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1 reference

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Factors influencing therapeutic efficacy and the host immune response to helper-dependent adenoviral gene therapy in hemophilia A mice

24 September 2018

1 reference

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Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice

24 September 2018

1 reference

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Correction of Bleeding Diathesis Without Liver Toxicity Using Arenaviral-Pseudotyped HIV-1–Based Vectors in Hemophilia A Mice

24 September 2018

1 reference

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Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.

24 September 2018

1 reference

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High-Level Factor VIII Gene ExpressionIn VivoAchieved by Nonviral Liver-Specific Gene Therapy Vectors

24 September 2018

1 reference

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Efficient production of human FVIII in hemophilic mice using lentiviral vectors

24 September 2018

1 reference

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In vitro and in vivo comparative study of chimeric liver-specific promoters

24 September 2018

1 reference

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Neonatal or hepatocyte growth factor-potentiated adult gene therapy with a retroviral vector results in therapeutic levels of canine factor IX for hemophilia B.

24 September 2018

1 reference

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Apical barriers to airway epithelial cell gene transfer with amphotropic retroviral vectors.

24 September 2018

1 reference

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Gene transfer to the brain using feline immunodeficiency virus-based lentivirus vectors

24 September 2018

1 reference

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In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.

24 September 2018

1 reference

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Incorporation of decay-accelerating factor into the baculovirus envelope generates complement-resistant gene transfer vectors

24 September 2018

1 reference

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Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

Systemic delivery of an adenoviral vector encoding canine factor VIII results in short-term phenotypic correction, inhibitor development, and biphasic liver toxicity in hemophilia A dogs.

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

Therapeutic levels of human factor VIII and IX using HIV-1-based lentiviral vectors in mouse liver

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

Prevention and treatment of factor VIII inhibitors in murine hemophilia A.

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A

24 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1895217

24 September 2018

1 reference

12 December 2020

Gene therapy for hemophilia

1 reference

PubMed

12 December 2020

Site-specific genomic integration produces therapeutic Factor IX levels in mice

1 reference

PubMed

12 December 2020

Mutagenesis of a Potential Immunoglobulin-binding Protein-binding Site Enhances Secretion of Coagulation Factor VIII

1 reference

PubMed

12 December 2020

10.1182/BLOOD-2004-11-4358

Identifiers

DOI

1 reference

10 August 2017

1 reference

10 August 2017

PubMed publication ID

15886327

1 reference