Intraosseous delivery of lentiviral vectors targeting factor VIII expression in platelets corrects murine hemophilia A. (Q35399235)

8 August 2017

title

Intraosseous delivery of lentiviral vectors targeting factor VIII expression in platelets corrects murine hemophilia A. (English)

1 reference

8 August 2017

0 references

Coagulation factor VIII

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hemophilia A

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author name string

Xuefeng Wang

1

1 reference

8 August 2017

Simon C Shin

2

1 reference

8 August 2017

Andy F J Chiang

3

1 reference

8 August 2017

Iram Khan

4

1 reference

8 August 2017

Dao Pan

5

1 reference

8 August 2017

David J Rawlings

6

1 reference

8 August 2017

Carol H Miao

7

1 reference

8 August 2017

publication date

6 February 2015

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8 August 2017

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8 August 2017

volume

23

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8 August 2017

issue

4

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8 August 2017

page(s)

617-626

1 reference

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

8 August 2017

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Syngeneic transplantation of hematopoietic stem cells that are genetically modified to express factor VIII in platelets restores hemostasis to hemophilia A mice with preexisting FVIII immunity

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12 July 2018

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12 July 2018

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12 July 2018

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Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion

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12 July 2018

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26 September 2018

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26 September 2018

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26 September 2018

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26 September 2018

1 reference

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Glycoprotein Ibalpha promoter drives megakaryocytic lineage-restricted expression after hematopoietic stem cell transduction using a self-inactivating lentiviral vector.

26 September 2018

1 reference

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Factor VIII ectopically expressed in platelets: efficacy in hemophilia A treatment

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4395783

Cost of care and quality of life for patients with hemophilia complicated by inhibitors: the COCIS Study Group

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4395783

In vivo retroviral gene transfer by direct intrafemoral injection results in correction of the SCID phenotype in Jak3 knock-out animals

26 September 2018

1 reference

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26 September 2018

1 reference

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Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.

26 September 2018

1 reference

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Gene transfer as an approach to treating hemophilia

26 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25655313

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Gene therapy in hemophilia: clinical trials update

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25655313

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/MT.2015.20

1 reference

8 August 2017

1 reference

8 August 2017

1 reference