Non-viral gene delivery in skeletal muscle: a protein factory (Q35061706)

6 August 2017

1 reference

title

Non-viral gene delivery in skeletal muscle: a protein factory (English)

1 reference

6 August 2017

Lu QL

1

1 reference

6 August 2017

Bou-Gharios G

series ordinal

2

1 reference

6 August 2017

Partridge TA

series ordinal

3

1 reference

6 August 2017

publication date

1 January 2003

1 reference

6 August 2017

1 reference

6 August 2017

volume

10

1 reference

6 August 2017

issue

2

1 reference

6 August 2017

page(s)

131-142

1 reference

Direct gene transfer into mouse muscle in vivo

6 August 2017

cites work

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Lentiviruses as gene transfer agents for delivery to non-dividing cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Herpes simplex virus vector-mediated dystrophin gene transfer and expression in MDX mouse skeletal muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Enhanced expression of recombinant dystrophin following intramuscular injection of Epstein-Barr virus (EBV)-based mini-chromosome vectors in mdx mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Optimised helper virus-free production of high-quality adeno-associated virus vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Overcoming adeno-associated virus vector size limitation through viral DNA heterodimerization

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Inflammatory responses following direct injection of plasmid DNA into skeletal muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene therapy for the treatment of hemophilia B using PINC-formulated plasmid delivered to muscle with electroporation

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Optimisation of electrotransfer of plasmid into skeletal muscle by pretreatment with hyaluronidase -- increased expression with reduced muscle damage

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Patterns of repair of dystrophic mouse muscle: studies on isolated fibers

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Invited review: myoblast transfer: a possible therapy for inherited myopathies?

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Muscle-derived hematopoietic stem cells are hematopoietic in origin

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Posttranslational modifications of recombinant myotube-synthesized human factor IX.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Long-term expression of erythropoietin in the systemic circulation of mice after intramuscular injection of a plasmid DNA vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Age and sex influence expression of plasmid DNA directly injected into mouse skeletal muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Optimization of transcriptional regulatory elements for constructing plasmid vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Multiple regions of the porcine alpha-skeletal actin gene modulate muscle-specific expression in cell culture and directly injected skeletal muscle.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Myosin light chain 3F regulatory sequences confer regionalized cardiac and skeletal muscle expression in transgenic mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Differential expression and secretion of alpha 1 anti-trypsin between direct DNA injection and implantation of transfected myoblast

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Analysis of tissue-specific gene delivery by recombinant adenoviruses containing cardiac-specific promoters

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Muscle-specific promoters may be necessary for adeno-associated virus-mediated gene transfer in the treatment of muscular dystrophies.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Massive idiosyncratic exon skipping corrects the nonsense mutation in dystrophic mouse muscle and produces functional revertant fibers by clonal expansion

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Muscle-specific enhancement of gene expression by incorporation of SV40 enhancer in the expression plasmid

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Kinetic analysis of translocation through nuclear pore complexes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Mutual exclusivity of DNA binding and nuclear localization signal recognition by the yeast transcription factor GAL4: implications for nonviral DNA delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Import of plasmid DNA into the nucleus is sequence specific

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Sequence requirements for plasmid nuclear import

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Prolonged transgene expression in glomeruli using an EBV replicon vector system combined with HVJ liposomes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Increased level and duration of expression in muscle by co-expression of a transactivator using plasmid systems

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Long-term control of erythropoietin secretion by doxycycline in mice transplanted with engineered primary myoblasts

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Regulated delivery of therapeutic proteins after in vivo somatic cell gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Tetracycline-regulated gene expression in the brain

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

A novel means of drug delivery: myoblast-mediated gene therapy and regulatable retroviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Transfection of cultured myoblasts in high serum concentration with DODAC:DOPE liposomes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Lipofection: a highly efficient, lipid-mediated DNA-transfection procedure

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Cellular and Molecular Barriers to Gene Transfer by a Cationic Lipid

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

On the mechanism whereby cationic lipids promote intracellular delivery of polynucleic acids

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Repeat administration of DNA/liposomes to the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Enhanced in vitro and in vivo cationic lipid-mediated gene delivery with a fluorinated glycerophosphoethanolamine helper lipid

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Targeting transgene expression for cystic fibrosis gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Cellular uptake of cationic lipid/DNA complexes by cultured myoblasts and myotubes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene therapy by intramuscular injection of plasmid DNA: studies on firefly luciferase gene expression in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Extracellular glycosaminoglycans modify cellular trafficking of lipoplexes and polyplexes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Interactions of mammalian cells with lipid dispersions containing novel metabolizable cationic amphiphiles

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Lipofection of cultured mouse muscle cells: a direct comparison of Lipofectamine and DOSPER.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene transfer with synthetic cationic amphiphiles: prospects for gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

A combination of poloxamers increases gene expression of plasmid DNA in skeletal muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Evaluation of polyether-polyethyleneimine graft copolymers as gene transfer agents.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

DNA transfection using linear poly(ethylenimine) prepared by controlled acid hydrolysis of poly(2-ethyl-2-oxazoline).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Transfection of large plasmids in primary human myoblasts.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Drug transporters revisited

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Sustained ex vivo and in vivo transfer of a reporter gene using polyoma virus pseudocapsids

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Adenovirus and adeno-associated virus mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Application of membrane-active peptides for drug and gene delivery across cellular membranes.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

DNA-binding transferrin conjugates as functional gene-delivery agents: synthesis by linkage of polylysine or ethidium homodimer to the transferrin carbohydrate moiety

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

pH-dependent bilayer destabilization by an amphipathic peptide

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Association of a pH-sensitive peptide with membrane vesicles: role of amino acid sequence

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Polyamidoamine cascade polymers mediate efficient transfection of cells in culture

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Design, synthesis, and characterization of a cationic peptide that binds to nucleic acids and permeabilizes bilayers.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

New basic membrane-destabilizing peptides for plasmid-based gene delivery in vitro and in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Translocating peptides and proteins and their use for gene delivery.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Synthetic DNA delivery systems

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Coupling of nuclear localization signals to plasmid DNA and specific interaction of the conjugates with importin alpha.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Improved packing of poly(ethylenimine)/DNA complexes increases transfection efficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene transfer into mammalian cells using histone-condensed plasmid DNA.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene transfer into muscle by electroporation in vivo.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

High-efficiency gene transfer into skeletal muscle mediated by electric pulses

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Gene therapy for streptozotocin-induced diabetic mice by electroporational transfer of naked human insulin precursor DNA into skeletal muscle in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Long-term production of erythropoietin after electroporation-mediated transfer of plasmid DNA into the muscles of normal and uremic rats.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

In vivo electroporation-mediated transfer of interleukin-12 and interleukin-18 genes induces significant antitumor effects against melanoma in mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Hyaluronidase enhances recombinant adeno-associated virus (rAAV)-mediated gene transfer in the rat skeletal muscle.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Tolerance, danger, and the extended family

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Electrotransfer of naked DNA in the skeletal muscles of animal models of muscular dystrophies

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Transfection of mammalian cells with plasmid DNA by scrape loading and sonication loading

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Microbubble-enhanced ultrasound for vascular gene delivery

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Ultrasound gene therapy: on the road from concept to reality.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

High-efficiency endovascular gene delivery via therapeutic ultrasound

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Ultrasound enhancement of liposome-mediated cell transfection is caused by cavitation effects.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Ultrasound enhancement of cationic lipid-mediated gene transfer to primary tumors following systemic administration

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Ultrasound facilitates transduction of naked plasmid DNA into colon carcinoma cells in vitro and in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Interactions between microbubbles and ultrasound: in vitro and in vivo observations

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

The efficient expression of intravascularly delivered DNA in rat muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Stable Expression of a Foreign Gene, Delivered by Gene Gun, in the Muscle of Rainbow Trout Oncorhynchus mykiss

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Nonviral in vivo gene delivery into tumors using a novel low volume jet-injection technology

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Role of the hepatitis B virus posttranscriptional regulatory element in export of intronless transcripts

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

Transcriptionally active drugs improve adenovirus vector performance in vitro and in vivo

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

HSV-1 amplicon vectors are a highly efficient gene delivery system for skeletal muscle myoblasts and myotubes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Interactions of cationic lipid vesicles with negatively charged phospholipid vesicles and biological membranes

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Intracellular Delivery of a Tat-eGFP Fusion Protein into Muscle Cells

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Polyvinyl derivatives as novel interactive polymers for controlled gene delivery to muscle

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Synergistic effect of formulated plasmid and needle-free injection for genetic vaccines

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Increased expression of DNA cointroduced with nuclear protein in adult rat liver

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Electric field mediated gene transfer

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Protection against autoimmune myocarditis by gene transfer of interleukin-10 by electroporation

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Efficient expression of naked dna delivered intraarterially to limb muscles of nonhuman primates

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Transfer of full-length Dmd to the diaphragm muscle of Dmd(mdx/mdx) mice through systemic administration of plasmid DNA

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301874

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3301874

1 reference

Dimensions Publication ID

6 August 2017

1032695009

0 references

1 reference