Lifetime correction of genetic deficiency in mice with a single injection of helper-dependent adenoviral vector (Q33949311)

30 July 2017

title

Lifetime correction of genetic deficiency in mice with a single injection of helper-dependent adenoviral vector (English)

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30 July 2017

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2

A Józkowicz

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30 July 2017

I H Kim

1

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30 July 2017

P A Piedra

series ordinal

3

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30 July 2017

K Oka

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4

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30 July 2017

L Chan

series ordinal

5

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30 July 2017

language of work or name

English

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publication date

30 October 2001

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Proceedings of the National Academy of Sciences of the United States of America

30 July 2017

published in

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30 July 2017

volume

98

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30 July 2017

issue

23

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30 July 2017

page(s)

13282-13287

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Long-term stable correction of low-density lipoprotein receptor-deficient mice with a helper-dependent adenoviral vector expressing the very low-density lipoprotein receptor

30 July 2017

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=60862

Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics

28 July 2018

1 reference

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Low levels of extrahepatic nonmacrophage ApoE inhibit atherosclerosis without correcting hypercholesterolemia in ApoE-deficient mice

28 July 2018

1 reference

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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

28 July 2018

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Administration of helper-dependent adenoviral vectors and sequential delivery of different vector serotype for long-term liver-directed gene transfer in baboons

28 July 2018

1 reference

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An adenoviral vector deleted for all viral coding sequences results in enhanced safety and extended expression of a leptin transgene

28 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=60862

A helper-dependent adenovirus vector system: removal of helper virus by Cre-mediated excision of the viral packaging signal

28 July 2018

1 reference

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In vivo muscle gene transfer of full-length dystrophin with an adenoviral vector that lacks all viral genes.

28 July 2018

1 reference

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Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells

28 July 2018

1 reference

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Adenovirus-mediated gene transfer: strategies and applications in lipoprotein research.

28 July 2018

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A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and beta-galactosidase

28 July 2018

1 reference

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Recombinant adenovirus deleted of all viral genes for gene therapy of cystic fibrosis

28 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=60862

Hypercholesterolemia in low density lipoprotein receptor knockout mice and its reversal by adenovirus-mediated gene delivery

28 July 2018

1 reference

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Rescue, propagation, and partial purification of a helper virus-dependent adenovirus vector

28 July 2018

1 reference

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A far-downstream hepatocyte-specific control region directs expression of the linked human apolipoprotein E and C-I genes in transgenic mice

28 July 2018

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A pilot study of ex vivo gene therapy for homozygous familial hypercholesterolaemia

28 July 2018

1 reference

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Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A.

28 July 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

Prolonged correction of hyperlipidemia in mice with familial hypercholesterolemia using an adeno-associated viral vector expressing very-low-density lipoprotein receptor.

21 January 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

Use of helper-dependent adenoviral vectors of alternative serotypes permits repeat vector administration

21 January 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

High doses of a helper-dependent adenoviral vector yield supraphysiological levels of alpha1-antitrypsin with negligible toxicity

21 January 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

Ex vivo gene transfer using adenovirus-mediated full-length dystrophin delivery to dystrophic muscles

21 January 2018

1 reference

https://api.crossref.org/works/10.1073/PNAS.241506298

Evaluation of the transfer and expression in mice of an enzyme-encoding gene using a human adenovirus vector

21 January 2018

1 reference

12 December 2020

Reversal of hypercholesterolemia in low density lipoprotein receptor knockout mice by adenovirus-mediated gene transfer of the very low density lipoprotein receptor

1 reference

12 December 2020

Determination of the lower threshold of apolipoprotein E resulting in remnant lipoprotein clearance

1 reference

12 December 2020

Adenoviral vector-mediated expression of physiologic levels of human factor VIII in nonhuman primates

1 reference

12 December 2020

Identifiers

DOI

10.1073/PNAS.241506298

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30 July 2017

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30 July 2017

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