AAV vectors: is clinical success on the horizon? (Q33840994)

29 July 2017

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title

AAV vectors: is clinical success on the horizon? (English)

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29 July 2017

Monahan PE

1

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29 July 2017

Samulski RJ

series ordinal

2

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29 July 2017

publication date

1 January 2000

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29 July 2017

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29 July 2017

volume

7

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29 July 2017

issue

1

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29 July 2017

page(s)

24-30

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NIDDK Workshop on AAV Vectors: Gene Transfer into Quiescent Cells

29 July 2017

cites work

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https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Gene transfer into hematopoietic progenitor cells mediated by an adeno-associated virus vector

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Progress in adeno-associated virus type 2 vector production: promises and prospects for clinical use.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Highly purified recombinant adeno-associated virus vectors are biologically active and free of detectable helper and wild-type viruses

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Viral receptors and vector purification: new approaches for generating clinical-grade reagents

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https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Titration of AAV-2 particles via a novel capsid ELISA: packaging of genomes can limit production of recombinant AAV-2.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Human fibroblast growth factor receptor 1 is a co-receptor for infection by adeno-associated virus 2.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Transduction and utility of the granulocyte-macrophage colony-stimulating factor gene into monocytes and dendritic cells by adeno-associated virus.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

High-titer adeno-associated viral vectors from a Rep/Cap cell line and hybrid shuttle virus

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I vector expressing AAV-2 Rep and Cap.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

In vitro packaging of an infectious recombinant adeno-associated virus 2

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Sustained correction of bleeding disorder in hemophilia B mice by gene therapy

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Insertional mutagenesis of AAV2 capsid and the production of recombinant virus

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Genetic capsid modifications allow efficient re-targeting of adeno-associated virus type 2.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Recombinant human parvovirus B19 vectors: erythroid cell-specific delivery and expression of transduced genes

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Efficient expression of CFTR function with adeno-associated virus vectors that carry shortened CFTR genes

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Concatamerization of adeno-associated virus circular genomes occurs through intermolecular recombination.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Recombinant adeno-associated virus for muscle directed gene therapy

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Latent adeno-associated virus infection elicits humoral but not cell-mediated immune responses in a nonhuman primate model

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Immune responses to adenovirus and adeno-associated virus in humans.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Infectious Clones and Vectors Derived from Adeno-Associated Virus (AAV) Serotypes Other Than AAV Type 2

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Nucleotide sequencing and generation of an infectious clone of adeno-associated virus 3.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Adeno-associated virus-mediated delivery of erythropoietin leads to sustained elevation of hematocrit in nonhuman primates

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Efficient and persistent gene transfer of AAV-CFTR in maxillary sinus

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Persistent expression of canine factor IX in hemophilia B canines

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3301109

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3301109

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29 July 2017

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