B cell-specific lentiviral gene therapy leads to sustained B-cell functional recovery in a murine model of X-linked agammaglobulinemia (Q33747337)

29 July 2017

title

B cell-specific lentiviral gene therapy leads to sustained B-cell functional recovery in a murine model of X-linked agammaglobulinemia (English)

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29 July 2017

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Hannah M Kerns

1

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29 July 2017

Byoung Y Ryu

2

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29 July 2017

Brigid V Stirling

3

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29 July 2017

Blythe D Sather

4

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29 July 2017

Alexander Astrakhan

5

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29 July 2017

Stephanie Humblet-Baron

6

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29 July 2017

Denny Liggitt

7

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29 July 2017

David J Rawlings

8

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29 July 2017

language of work or name

English

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publication date

21 January 2010

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29 July 2017

number of pages

10

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inferred from page(s)

published in

Blood

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29 July 2017

volume

115

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29 July 2017

issue

11

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29 July 2017

page(s)

2146-2155

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Insertional transformation of hematopoietic cells by self-inactivating lentiviral and gammaretroviral vectors

29 July 2017

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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A novel mutation (Cys145-->Stop) in Bruton's tyrosine kinase is associated with newly diagnosed X-linked agammaglobulinemia in a 51-year-old male.

21 June 2018

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21 June 2018

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Analysis of the Bruton's tyrosine kinase gene promoter reveals critical PU.1 and SP1 sites

21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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Sustained correction of B-cell development and function in a murine model of X-linked agammaglobulinemia (XLA) using retroviral-mediated gene transfer

21 June 2018

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30 October 2018

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30 October 2018

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30 October 2018

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30 October 2018

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Long-term chimerism and B-cell function after bone marrow transplantation in patients with severe combined immunodeficiency with B cells: A single-center study of 22 patients

30 October 2018

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A Btk transgene restores the antiviral TI-2 antibody responses of xid mice in a dose-dependent fashion

30 October 2018

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Early arrest in B cell development in transgenic mice that express the E41K Bruton's tyrosine kinase mutant under the control of the CD19 promoter region.

30 October 2018

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30 October 2018

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30 October 2018

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Expression of the gene defect in X-linked agammaglobulinemia

30 October 2018

1 reference

12 December 2020

Transcriptional regulatory elements within the first intron of Bruton's tyrosine kinase

1 reference

12 December 2020

The health status and quality of life of adults with X-linked agammaglobulinemia

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12 December 2020

X-linked agammaglobulinemia: report on a United States registry of 201 patients

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12 December 2020

Competition within the early B-cell compartment conditions B-cell reconstitution after hematopoietic stem cell transplantation in nonirradiated recipients

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12 December 2020

Gene therapy of inherited immunodeficiencies

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12 December 2020

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12 December 2020

10.1182/BLOOD-2009-09-241869

Identifiers

DOI

1 reference

release_7iwdqdsda5cr5k5zps5bguv7wu

29 July 2017

Fatcat ID

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Fatcat

https://api.fatcat.wiki/v0/release/7iwdqdsda5cr5k5zps5bguv7wu

24 November 2022

mapped directly with Wikidata item

PMC publication ID

2844021

1 reference

29 July 2017

1 reference