Comparison of factor VIII transgenes bioengineered for improved expression in gene therapy of hemophilia A (Q33688429)

28 July 2017

title

Comparison of factor VIII transgenes bioengineered for improved expression in gene therapy of hemophilia A (English)

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28 July 2017

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Coagulation factor VIII

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hemophilia A

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author name string

Kerry L Dooriss

1

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28 July 2017

Gabriela Denning

2

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28 July 2017

Bagirath Gangadharan

3

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28 July 2017

Elisabeth H Javazon

4

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28 July 2017

David A McCarty

5

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28 July 2017

H Trent Spencer

6

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28 July 2017

Christopher B Doering

7

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28 July 2017

publication date

1 May 2009

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28 July 2017

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28 July 2017

volume

20

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28 July 2017

issue

5

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28 July 2017

page(s)

465-478

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describes a project that uses

28 July 2017

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC2828624/fullTextXML

based on heuristic

inferred from PubMed Central ID database lookup

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Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors

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30 October 2018

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30 October 2018

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30 October 2018

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Correction of Bleeding Diathesis Without Liver Toxicity Using Arenaviral-Pseudotyped HIV-1–Based Vectors in Hemophilia A Mice

30 October 2018

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30 October 2018

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Sustained human factor VIII expression in hemophilia A mice following systemic delivery of a gutless adenoviral vector

30 October 2018

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Sustained high-level expression of full-length human factor VIII and restoration of clotting activity in hemophilic mice using a minimal adenovirus vector.

30 October 2018

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Reduction of the antigenicity of factor VIII toward complex inhibitory antibody plasmas using multiply-substituted hybrid human/porcine factor VIII molecules.

30 October 2018

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Biochemical, immunological, and in vivo functional characterization of B-domain-deleted factor VIII.

30 October 2018

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PubMed

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based on heuristic

Mutagenesis of a Potential Immunoglobulin-binding Protein-binding Site Enhances Secretion of Coagulation Factor VIII

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19222367

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1089/HUM.2008.150

1 reference

28 July 2017

1 reference

28 July 2017

1 reference