Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene (Q33633266)

28 July 2017

title

Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene (English)

1 reference

28 July 2017

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Charles Harvey Vannoy

1

1 reference

28 July 2017

Will Xiao

2

1 reference

28 July 2017

Peijuan Lu

3

1 reference

28 July 2017

Xiao Xiao

4

1 reference

28 July 2017

Qi Long Lu

5

1 reference

28 July 2017

publication date

8 March 2017

1 reference

Molecular Therapy. Methods & Clinical Development

28 July 2017

published in

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28 July 2017

volume

5

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28 July 2017

page(s)

31-42

1 reference

describes a project that uses

28 July 2017

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC5415313/fullTextXML

based on heuristic

inferred from PubMed Central ID database lookup

cites work

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21 June 2018

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Adeno-associated virus 9 mediated FKRP gene therapy restores functional glycosylation of α-dystroglycan and improves muscle functions

21 June 2018

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Mutations in ISPD cause Walker-Warburg syndrome and defective glycosylation of α-dystroglycan

21 June 2018

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21 June 2018

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21 June 2018

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Mutations in the fukutin-related protein gene (FKRP) cause a form of congenital muscular dystrophy with secondary laminin alpha2 deficiency and abnormal glycosylation of alpha-dystroglycan

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30 October 2018

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PubMed

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inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1016/J.OMTM.2017.02.002

1 reference

28 July 2017

1 reference

28 July 2017

1 reference