Our team was excited to attend the 2024 Phelan-McDermid Syndrome Foundation Family Conference last week in Minneapolis! We appreciated meeting and talking with families about their loved ones. We also had the opportunity to present information about our JAG201 program targeting #SHANK3 haploinsufficiency. Thank you to everyone who welcomed us, listened to our presentation and shared their stories with us. To learn more about how Jaguar is accelerating breakthroughs in gene therapies for those living with severe genetic diseases, visit: www.jaguargenetherapy.com #pmsfconference2024
Jaguar Gene Therapy
Biotechnology Research
Lake Forest, IL 10,966 followers
Jaguar Gene Therapy is accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases.
About us
Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable patient populations. The company is made up of a proven team of experts with unparalleled CMC (Chemistry, Manufacturing and Controls), regulatory, clinical and commercial acumen who have first-hand experience in bringing novel gene therapy treatments to patients and their families. Committed to patient safety and product purity, Jaguar is rapidly advancing an initial pipeline of three programs targeting: 1) Type 1 galactosemia; 2) a genetic cause of autism spectrum disorder and Phelan-McDermid syndrome and other severe neurodevelopmental disorders with a SHANK3 mutation or deletion; and 3) Type 1 diabetes. The company continues to evaluate opportunities to expand its pipeline using the strength of the team and close relationships with numerous academic institutions.
- Website
-
http://www.jaguargenetherapy.com
External link for Jaguar Gene Therapy
- Industry
- Biotechnology Research
- Company size
- 51-200 employees
- Headquarters
- Lake Forest, IL
- Type
- Privately Held
- Founded
- 2019
- Specialties
- Biotechnology, Severe Genetic Diseases, and Gene Therapy
Locations
-
Primary
Get directions
Lake Forest, IL, US
-
Get directions
Cary, NC, US
Employees at Jaguar Gene Therapy
Updates
-
This morning, we issued a press release to share updates on our JAG201 program targeting a genetic form of #autism spectrum disorder and #Phelan-McDermid syndrome. Read the full release here: https://lnkd.in/giezNAZm #SHANK3 #phelanmcdermid
-
-
Thanks to Michael Hughes for presenting preclinical data on our SHANK3 program at #ASGCT2024. For more information about our pipeline programs, visit: www.jaguargenetherapy.com.
-
Honored to be named a “Company of the Year” by CureSHANK during their #PMSDDS last week. We are inspired by the Phelan-McDermid syndrome community and grateful for the insights and experiences they’ve shared with us. Thank you, CureSHANK, for this recognition – we are sincerely touched. #SHANK3 #phelanmcdermidsyndrome #phelanmcdermid
Congratulations to Jaguar Gene Therapy, a recipient of the CureSHANK "Company of the Year" award, presented during our inaugural PMS Drug Development Symposium (#PMSDDS) in Boston last week! Receiving the award on behalf of Jaguar were CEO Joseph Nolan and Daniel Gallo, PhD, Head of Medical Affairs. We are so thankful that Jaguar has prioritized its JAG-201 program, pioneering the first SHANK3 mini-gene replacement therapy for PMS and recently receiving an IND to begin clinical trials! The Jaguar team is a pleasure to work with and shows Jaguar's great commitment to improving patient quality of life. [These #pmsdds2024 posts are trickling in because CureSHANK is a shoestring operation with a skeleton crew mostly composed of parents caring for disabled children with PMS. To help us in our work, keep an eye out for our "Raise for Research" fundraiser, running next week May 6-10!] Pictured left to right: CureSHANK president and co-founder Geraldine Bliss; Joe Nolan; Dan Gallo. #phelanmcdermidsyndrome #phelanmcdermid #shank3 #raiseforresearch
-
-
Yesterday, our team was happy to present an analysis that provides additional insights into the real-world burden of #galactosemia among U.S. children, adolescents and adults at the 45th Annual Meeting of the Society for Inherited Metabolic Disorders. For more information about galactosemia, visit Galactosemia Foundation: www.galactosemia.org
Galactosemia Foundation
galactosemia.org
-
April is World #Autism Month. To learn more, we encourage you to visit: https://lnkd.in/gJ2teRx.
World Autism Month | Autism Speaks
autismspeaks.org
-
Proud to show our support for #PhelanLucky, an awareness and fundraising campaign held by Phelan-McDermid Syndrome Foundation . To learn more about the campaign, the foundation and #PhelanMcDermid syndrome, visit: https://lnkd.in/e_VhFMtC. #shank3 #phelanmcdermidsyndrome
Phelan Lucky
https://pmsf.org
-
To mark #RareDiseaseDay this year, we encourage you to learn more about the rare diseases #PhelanMcDermidsyndrome and #galactosemia. Connect with Phelan-McDermid Syndrome Foundation and CureSHANK for information on #phelanmcdermid and with Galactosemia Foundation for galactosemia information. You can learn more about Rare Disease Day here: https://lnkd.in/gk6hbAF
Rare Disease Day 2024
https://www.rarediseaseday.org
-
Yesterday, our CEO Joseph Nolan joined a panel discussion at Biotechnology Innovation Organization’s CEO & Investor Conference in New York. Along with two other panelists, Joe shared his insights on scalability and access for gene therapies now and in the future. Learn more about Joe and the Jaguar team: https://lnkd.in/ggAvhmFF Photo credit: Biotechnology Innovation Organization #BIOCEO24
Home
https://jaguargenetherapy.com
-
Sharing this opportunity from Galactosemia Foundation to provide feedback on the new #galactosemia handbook that was released last year.
We are seeking feedback from the #galactosemia community! Have you read the handbook we launched in June of 2022? We want your thoughts on the usefulness of this resource. If you’re interested, take a brief survey to tell us what you think! It’s only 15 questions and will take no more than 30 minutes to complete: https://lnkd.in/e6XeCiRP
-