Inozyme Pharma

We are proud to share a thought-provoking op-ed by our COO, Matt Winton, Ph.D., in BioSpace. In this article, he discusses the critical need for Congress to reauthorize the FDA’s Priority Review Voucher (PRV) program. This program is crucial for advancing the development of life-saving treatments for children suffering from rare diseases. The reauthorization will ensure continued support for innovative research and drug development, directly impacting the lives of our youngest and most vulnerable patients. At Inozyme, we are committed to addressing the unmet needs of patients with rare diseases, and this op-ed highlights the importance of sustained legislative support in achieving our mission. The FDA's pediatric rare disease program has been instrumental in bringing new therapies to market, offering hope and improved outcomes for countless families. Matt joined other biopharmaceutical leaders last week in Washington, D.C., as part of a delegation of The Rare Disease Company Coalition to discuss the PRV program's impact on drug development for pediatric rare diseases Join us in advocating for this vital initiative by reading the full article and learning more about the impact and significance of this program. Together, we can make a difference in the lives of children with #RareDiseases. Read the full article: https://bit.ly/3zA36oP #PriorityReviewVoucher #Biotech #Biopharmaceutical

We were honored to join Senator Amy Klobuchar today to discuss the best ways to support the millions of Americans living with the #raredisease - including the reauthorization of the #PriorityReviewVoucher program. We are so thankful to the Senator for her commitment to the rare disease community, including her leadership in the Rare Disease Caucus. Thanks for your time today, Senator! Reenie McCarthy, Rebecca Michalski McLeod, Adora Ndu, Steven Pfanstiel, Stuart Siedman, Izabella (Izzy) Tyszler, Matt Winton, Stacey Frisk

Our Women in Progress (WIP) team recently hosted an informative seminar led by Brad Johnson and David Smith, co-authors of the acclaimed book "Good Guys: How Men Can Be Better Allies for Women in the Workplace."     The interactive session delved into practical strategies for creating a more inclusive work environment through the power of effective allyship.      Attendees actively participated by applying these concepts to scenarios specific to Inozyme, generating lively discussions. We left the event well-equipped with valuable tools and a renewed perspective to promote a more equitable workplace for all.     #InozymeWIP #Allyship #WorkplaceInclusion

We are proud to share this published article from our colleagues, which highlights how INZ-701 can prevent intimal proliferation (excessive cell growth within blood vessel walls). This overgrowth can obstruct blood flow and increase the risk of cardiovascular events like heart attacks and strokes. The research broadens potential therapeutic applications of INZ-701 beyond enzyme replacement therapy in our three ongoing clinical programs in ENPP1 Deficiency, ABCC6 Deficiency, and calciphylaxis, where morbidity and mortality can be driven by intimal proliferation. Read the research here: https://bit.ly/3XRS4W6

Today, we announced that the FDA has granted INZ-701 Fast Track designation for the treatment of #ABCC6 Deficiency. The Fast Track program gives us the opportunity to expedite the development of INZ-701 to potentially treat pediatric patients quicker with an efficient path to approval. Learn more: https://bit.ly/3RM9v6v #RareDisease #Biotech #Biopharmaceutical  

Congratulations to our partner, Leanne Ward, M.D., Professor of Pediatrics in the Faculty of Medicine, University of Ottawa, for receiving the Gold Award this week for her excellent presentation at the International Society for Children's Bone Health International Conference. Dr. Ward presented important data from our radiographic study describing skeletal features of children with #ENPP1 Deficiency. #ICCBH2024

Celebrated every year on June 28, International Neonatal Screening Day is vital in promoting earlier access to treatment, which can significantly improve health outcomes for newborns.    #NewbornScreening can accelerate detection and early intervention for #RareDiseases like #ENPP1 and #ABCC6 Deficiencies.     Through our collaboration with partners, we strive to ensure families have access to these potentially life-saving tools.    #NeonatalScreeningMatters #INSD

Doug Treco, Ph.D., our CEO and chairman, discussed our Phase 1/2 clinical trials for INZ-701 in adults with #ENPP1 Deficiency and #ABCC6 Deficiency during a recent interview with CheckRare. Doug walked through the latest data from these trials and emphasized the importance of patient identification and community relationships. Learn more: https://bit.ly/3x0LX6Z #Biotech #Biopharmaceutical

Our team is excited to attend and support the International Society for Children's Bone Health 11th International Conference this week in Salzburg, Austria. It is a significant event each year in the field of pediatric bone health. Leanne Ward, M.D., Professor of Pediatrics in the Faculty of Medicine, University of Ottawa, will present data from our radiographic study describing skeletal features of children with #ENPP1 Deficiency on Monday, June 24, at 11 a.m. CEST. Several members of our leadership team will be in attendance as well to discuss our clinical and regulatory efforts. Learn more: https://bit.ly/3VrXi8g #ICCBH2024

This #PrideMonth, we proudly reaffirm our unwavering dedication to an inclusive workplace culture that celebrates and respects all individuals.   Our team encourages authentic perspectives and collaboration to deliver on our commitment to restoring health and hope to individuals with #RareDiseases.    #Pride2024